Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
Title:
Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
Author:
Esposito, Federica Dell’Aquila, Fabio Rhiel, Manuel Auricchio, Stefano Chmielewski, Kay Ole Andrieux, Geoffroy Ferla, Rita Horrach, Paula Sureda Padmanabhan, Arjun Di Cunto, Roberto Notaro, Simone Santeularia, Manel Llado Boerries, Melanie Dell’Anno, Margherita Nusco, Edoardo Padula, Agnese Nutarelli, Sofia Cornu, Tatjana I. Sorrentino, Nicolina Cristina Piccolo, Pasquale Trapani, Ivana Cathomen, Toni Auricchio, Alberto