A FIRST-IN-HUMAN FOUR-YEAR FOLLOW-UP STUDY OF DURABLE THERAPEUTIC EFFICACY AND SAFETY OF AAV GENE THERAPY WITH VALOCTOCOGENE ROXAPARVOVEC FOR SEVERE HEMOPHILIA A
Titel:
A FIRST-IN-HUMAN FOUR-YEAR FOLLOW-UP STUDY OF DURABLE THERAPEUTIC EFFICACY AND SAFETY OF AAV GENE THERAPY WITH VALOCTOCOGENE ROXAPARVOVEC FOR SEVERE HEMOPHILIA A
Auteur:
Ozelo, M.C. Pasi, K.J. Rangarajan, S. Mitchell, N. Lester, W. Symington, E. Madan, B. Laffan, M. Russell, C.B. Li, M. Kim, B. Pierce, G.F. Wong, W.Y.