Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial
Titel:
Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial
Auteur:
Savarirayan, Ravi Wilcox, William R Harmatz, Paul Phillips III, John Polgreen, Lynda E Tofts, Louise Ozono, Keiichi Arundel, Paul Irving, Melita Bacino, Carlos A Basel, Donald Bober, Michael B Charrow, Joel Mochizuki, Hiroshi Kotani, Yumiko Saal, Howard M Army, Clare Jeha, George Qi, Yulan Han, Lynn Fisheleva, Elena Huntsman-Labed, Alice Day, Jonathan