Effect of alglucosidase alfa dosage on survival and walking ability in patients with classic infantile Pompe disease: a multicentre observational cohort study from the European Pompe Consortium
Titel:
Effect of alglucosidase alfa dosage on survival and walking ability in patients with classic infantile Pompe disease: a multicentre observational cohort study from the European Pompe Consortium
Auteur:
Ditters, Imke Anne Maartje Huidekoper, Hidde Harmen Kruijshaar, Michelle Elisabeth Rizopoulos, Dimitris Hahn, Andreas Mongini, Tiziana Enrica Labarthe, François Tardieu, Marine Chabrol, Brigitte Brassier, Anais Parini, Rossella Parenti, Giancarlo van der Beek, Nadine Anna Maria Elisabeth van der Ploeg, Ans Tjitske van den Hout, Johanna Maria Pieternel