Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1
Titel:
Randomized Clinical Trial on the Long-Term Efficacy and Safety of Lumasiran in Patients With Primary Hyperoxaluria Type 1
Auteur:
Hulton, Sally A. Groothoff, Jaap W. Frishberg, Yaacov Koren, Michael J. Overcash, J. Scott Sellier-Leclerc, Anne-Laure Shasha-Lavsky, Hadas Saland, Jeffrey M. Hayes, Wesley Magen, Daniella Moochhala, Shabbir H. Coenen, Martin Simkova, Eva Garrelfs, Sander F. Sas, David J. Meliambro, Kristin A. Ngo, Taylor Sweetser, Marianne T. Habtemariam, Bahru A. Gansner, John M. McGregor, Tracy L. Lieske, John C.