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Efficacy and preliminary safety assessment of EXG001-307 AAV gene therapy for spinal muscular atrophy |
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Titel: |
Efficacy and preliminary safety assessment of EXG001-307 AAV gene therapy for spinal muscular atrophy |
Auteur: |
Song, Chunjuan Wang, Qingzeng Zhu, Peixin Li, Junhui Dai, Li Hu, Wei Yang, Wenshu Zhang, Runyuan Wang, Dandan Li, Zhongwan Chen, Shuyuan Wang, Lijun Ye, Guojie Wu, Zhenhua |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 33 () nr. 2 pagina's p. |
Jaar: |
2025 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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