An in vitro and in vivo efficacy evaluation of gene therapy candidate SBT101 in mouse models of adrenomyeloneuropathy and in NHPs
Titel:
An in vitro and in vivo efficacy evaluation of gene therapy candidate SBT101 in mouse models of adrenomyeloneuropathy and in NHPs
Auteur:
Vasireddy, Vidyullatha Maguire, Casey A. Anderson, David W. Ng, Carrie Gong, Yi Eichler, Florian Fourcade, Stéphane Guilera, Cristina Onieva, Andrea Sanchez, Angela Leal-Julià, Marc Verdés, Sergi Dijkstra, Inge M.E. Kemp, Stephan Park, HongGeun Lutz, Tiffany Clark, Sean W. Bosch, Assumpció Pujol, Aurora Kozarsky, Karen