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A GLB1 transgene with enhanced therapeutic potential for the preclinical development of ex-vivo gene therapy to treat mucopolysaccharidosis type IVB |
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Titel: |
A GLB1 transgene with enhanced therapeutic potential for the preclinical development of ex-vivo gene therapy to treat mucopolysaccharidosis type IVB |
Auteur: |
Crippa, Stefania Alberti, Gaia Passerini, Laura Savoia, Evelyn Oliva Mancino, Marilena De Ponti, Giada Santi, Ludovica Berti, Margherita Testa, Marialuisa Hernandez, Raisa Jofra Quaranta, Pamela Ceriotti, Selene Visigalli, Ilaria Morrone, Amelia Paoli, Antonella Forni, Claudia Scala, Serena Degano, Massimo Staiano, Leopoldo Gregori, Silvia Aiuti, Alessandro Bernardo, Maria Ester |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 32 () nr. 3 pagina's p. |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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