A novel high-titer, bifunctional lentiviral vector for autologous hematopoietic stem cell gene therapy of sickle cell disease
Titel:
A novel high-titer, bifunctional lentiviral vector for autologous hematopoietic stem cell gene therapy of sickle cell disease
Auteur:
Hart, Kevyn L. Liu, Boya Brown, Devin Campo-Fernandez, Beatriz Tam, Kevin Orr, Katherine Hollis, Roger P. Brendel, Christian Williams, David A. Kohn, Donald B.