A blood-brain barrier-penetrant AAV gene therapy improves neurological function in symptomatic mucolipidosis IV mice
Titel:
A blood-brain barrier-penetrant AAV gene therapy improves neurological function in symptomatic mucolipidosis IV mice
Auteur:
Sangster, Madison L. Bishop, Martha M. Yao, Yizheng Feitor, Jessica F. Shahriar, Sanjid Miller, Maxwell E. Chekuri, Anil K. Budnik, Bogdan Bei, Fengfeng Grishchuk, Yulia