Whole-body galactose oxidation as a robust functional assay to assess the efficacy of gene-based therapies in a mouse model of Galactosemia
Titel:
Whole-body galactose oxidation as a robust functional assay to assess the efficacy of gene-based therapies in a mouse model of Galactosemia
Auteur:
Balakrishnan, Bijina Yan, Xinhua McCue, Marshall D. Bellagamba, Olivia Guo, Aaron Winkler, Felicity Thall, Jason Crawford, Lisa Dimen, Rain Chen, Sara McEnaney, Sean Wu, Yiman Zimmer, Mike Sarkis, Joe Martini, Paolo G.V. Finn, Patrick F. Lai, Kent