Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR-Cas9 gene editing
Titel:
Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR-Cas9 gene editing
Auteur:
Walker, Amy J. Graham, Carina Greenwood, Miriam Woodall, Maximillian Maeshima, Ruhina O’Hara-Wright, Michelle Sanz, David J. Guerrini, Ileana Aldossary, Ahmad M. O’Callaghan, Christopher Baines, Deborah L. Harrison, Patrick T. Hart, Stephen L.