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CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice |
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Titel: |
CRISPR-Cas9-mediated somatic correction of a one-base deletion in the Ugt1a gene ameliorates hyperbilirubinemia in Crigler-Najjar syndrome mice |
Auteur: |
Bortolussi, Giulia Iaconcig, Alessandra Canarutto, Giulia Porro, Fabiola Ferrucci, Filippo Galletta, Claudia Díaz-Muñoz, Cristian Rawat, Vipin De Caneva, Alessia Olajide, Olayemi Joseph Zentilin, Lorena Piazza, Silvano Bočkor, Luka Muro, Andrés Fernando |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 31 () nr. C pagina's p. |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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