Systemic gene therapy using an AAV44.9 vector rescues a neonatal lethal mouse model of propionic acidemia
Titel:
Systemic gene therapy using an AAV44.9 vector rescues a neonatal lethal mouse model of propionic acidemia
Auteur:
Chandler, Randy J. Di Pasquale, Giovanni Choi, Eun-Young Chang, David Smith, Stephanie N. Sloan, Jennifer L. Hoffmann, Victoria Li, Lina Chiorini, John A. Venditti, Charles P.