Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping
Titel:
Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping
Auteur:
Rok, Matthew Wong, Tatianna Wai Ying Maino, Eleonora Ahmed, Abdalla Yang, Grace Hyatt, Elzbieta Lindsay, Kyle Fatehi, Sina Marks, Ryan Delgado-Olguín, Paul Ivakine, Evgueni A. Cohn, Ronald D.