Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation
Titel:
Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation
Auteur:
Corti, Manuela Byrne, Barry J. Gessler, Dominic J. Thompson, Grace Norman, Samantha Lammers, Jenna Coleman, Kirsten E. Liberati, Cristina Elder, Melissa E. Escolar, Maria L. Tuna, Ibrahim S. Mesaros, Clementina Kleiner, Gary I. Barbouth, Deborah S. Gray-Edwards, Heather L. Clement, Nathalie Cleaver, Brian D. Gao, Guangping