Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution
Titel:
Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution
Auteur:
Cabanes-Creus, Marti Navarro, Renina Gale Liao, Sophia H.Y. Scott, Suzanne Carlessi, Rodrigo Roca-Pinilla, Ramon Knight, Maddison Baltazar, Grober Zhu, Erhua Jones, Matthew Denisenko, Elena Forrest, Alistair R.R. Alexander, Ian E. Tirnitz-Parker, Janina E.E. Lisowski, Leszek