Systemic γ-sarcoglycan AAV gene transfer results in dose-dependent correction of muscle deficits in the LGMD 2C/R5 mouse model
Titel:
Systemic γ-sarcoglycan AAV gene transfer results in dose-dependent correction of muscle deficits in the LGMD 2C/R5 mouse model
Auteur:
Seo, Young-Eun Baine, Stephen H. Kempton, Amber N. Rogers, Oliver C. Lewis, Sarah Adegboye, Kaitlin Haile, Alex Griffin, Danielle A. Peterson, Ellyn L. Pozsgai, Eric R. Potter, Rachael A. Rodino-Klapac, Louise R.