Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B
Titel:
Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B
Auteur:
Ferla, Rita Dell’Aquila, Fabio Doria, Monica Ferraiuolo, Maria Noto, Alessia Grazioli, Fabiana Ammendola, Virginia Testa, Francesco Melillo, Paolo Iodice, Carolina Risca, Giulia Tedesco, Novella le Brun, Pierre Romain Surace, Enrico Maria Simonelli, Francesca Galimberti, Stefania Valsecchi, Maria Grazia Marteau, Jean-Brice Veron, Philippe Colloca, Stefano Auricchio, Alberto