Young mice administered adult doses of AAV5-hFVIII-SQ achieve therapeutic factor VIII expression into adulthood
Titel:
Young mice administered adult doses of AAV5-hFVIII-SQ achieve therapeutic factor VIII expression into adulthood
Auteur:
Zhang, Lening Yates, Bridget Murphy, Ryan Liu, Su Xie, Lin Handyside, Britta Sihn, Choong-Ryoul Bouwman, Taren Galicia, Nicole Tan, Danielle Fonck, Carlos Arens, Jeremy Clark, Annie Zhang, Weiming Chandra, Sundeep Srimani, Jaydeep Holcomb, Jennifer Van Tuyl, Andrea Henshaw, Joshua Vettermann, Christian Siso, Silvia Su, Cheng Bullens, Sherry Bunting, Stuart O’Neill, Charles Fong, Sylvia