Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities
Titel:
Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities
Auteur:
Khoja, Suhail Lambert, Jenna Nitzahn, Matthew Eliav, Adam Zhang, YuChen Tamboline, Mikayla Le, Colleen T. Nasser, Eram Li, Yunfeng Patel, Puja Zhuravka, Irina Lueptow, Lindsay M. Tkachyova, Ilona Xu, Shili Nissim, Itzhak Schulze, Andreas Lipshutz, Gerald S.