Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette
Titel:
Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette
Auteur:
Kumar, Sandeep R.P. Xie, Jun Hu, Shilang Ko, Jihye Huang, Qifeng Brown, Harrison C. Srivastava, Alok Markusic, David M. Doering, Christopher B. Spencer, H. Trent Srivastava, Arun Gao, Guangping Herzog, Roland W.