Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal
Titel:
Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal
Auteur:
Marcó, Sara Haurigot, Virginia Jaén, Maria Luisa Ribera, Albert Sánchez, Víctor Molas, Maria Garcia, Miguel León, Xavier Roca, Carles Sánchez, Xavier Bertolin, Joan Pérez, Jennifer Elias, Gemma Navarro, Marc Carretero, Ana Pumarola, Martí Andaluz, Anna Espada, Yvonne Añor, Sonia Bosch, Fatima