In vivo genome editing at the albumin locus to treat methylmalonic acidemia
Titel:
In vivo genome editing at the albumin locus to treat methylmalonic acidemia
Auteur:
Schneller, Jessica L. Lee, Ciaran M. Venturoni, Leah E. Chandler, Randy J. Li, Ang Myung, Sangho Cradick, Thomas J. Hurley, Ayrea E. Lagor, William R. Bao, Gang Venditti, Charles P.