AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder
Titel:
AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder
Auteur:
Argyriou, Catherine Polosa, Anna Song, Ji Yun Omri, Samy Steele, Bradford Cécyre, Bruno McDougald, Devin S. Di Pietro, Erminia Bouchard, Jean-François Bennett, Jean Hacia, Joseph G. Lachapelle, Pierre Braverman, Nancy E.