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Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device |
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Titel: |
Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device |
Auteur: |
Olgasi, Cristina Borsotti, Chiara Merlin, Simone Bergmann, Thorsten Bittorf, Patrick Adewoye, Adeolu Badi Wragg, Nicholas Patterson, Kelcey Calabria, Andrea Benedicenti, Fabrizio Cucci, Alessia Borchiellini, Alessandra Pollio, Berardino Montini, Eugenio Mazzuca, Delfina M. Zierau, Martin Stolzing, Alexandra Toleikis, Philip.M. Braspenning, Joris Follenzi, Antonia |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 23 () nr. C pagina's 551-566 |
Jaar: |
2021 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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