Preclinical studies of efficacy thresholds and tolerability of a clinically ready lentiviral vector for pyruvate kinase deficiency treatment
Titel:
Preclinical studies of efficacy thresholds and tolerability of a clinically ready lentiviral vector for pyruvate kinase deficiency treatment
Auteur:
Navarro, Susana Quintana-Bustamante, Oscar Sanchez-Dominguez, Rebeca Lopez-Manzaneda, Sergio Ojeda-Perez, Isabel Garcia-Torralba, Aida Alberquilla, Omaira Law, Kenneth Beard, Brian C. Bastone, Antonella Rothe, Michael Villanueva, Mariela Ramirez, Juan C. Fañanas-Baquero, Sara Nieto-Romero, Virginia Molinos-Vicente, Andrea Gutierrez, Sonia Nicoletti, Eileen García-Bravo, María Bueren, Juan A. Schwartz, Jonathan D. Segovia, Jose-Carlos