ImmTOR nanoparticles enhance AAV transgene expression after initial and repeat dosing in a mouse model of methylmalonic acidemia
Titel:
ImmTOR nanoparticles enhance AAV transgene expression after initial and repeat dosing in a mouse model of methylmalonic acidemia
Auteur:
Ilyinskii, Petr O. Michaud, Alicia M. Rizzo, Gina L. Roy, Christopher J. Leung, Sheldon S. Elkins, Stephanie L. Capela, Teresa Chowdhury, Aparajita Li, Lina Chandler, Randy J. Manoli, Irini Andres-Mateos, Eva Johnston, Lloyd P.M. Vandenberghe, Luk H. Venditti, Charles P. Kishimoto, Takashi Kei