|
Systemic Treatment of Fabry Disease Using a Novel AAV9 Vector Expressing α-Galactosidase A |
|
|
|
Titel: |
Systemic Treatment of Fabry Disease Using a Novel AAV9 Vector Expressing α-Galactosidase A |
Auteur: |
Biferi, Maria Grazia Cohen-Tannoudji, Mathilde García-Silva, Andrea Souto-Rodríguez, Olga Viéitez-González, Irene San-Millán-Tejado, Beatriz Fernández-Carrera, Andrea Pérez-Márquez, Tania Teijeira-Bautista, Susana Barrera, Soraya Domínguez, Vanesa Marais, Thibaut González-Fernández, África Barkats, Martine Ortolano, Saida |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 20 () nr. C pagina's 1-17 |
Jaar: |
2021 |
Inhoud: |
|
Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
|
|
|
|