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Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector |
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Titel: |
Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector |
Auteur: |
De Sabbata, Giulia Boisgerault, Florence Guarnaccia, Corrado Iaconcig, Alessandra Bortolussi, Giulia Collaud, Fanny Ronzitti, Giuseppe Sola, Marcelo Simon Vidal, Patrice Rouillon, Jeremy Charles, Severine Nicastro, Emanuele D’Antiga, Lorenzo Ilyinskii, Petr Mingozzi, Federico Kishimoto, Takashi Kei Muro, Andrés F. |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 20 () nr. C pagina's 169-180 |
Jaar: |
2021 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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