Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice
Titel:
Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice
Auteur:
White, Katherine A. Nelvagal, Hemanth R. Poole, Timothy A. Lu, Bin Johnson, Tyler B. Davis, Samantha Pratt, Melissa A. Brudvig, Jon Assis, Ana B. Likhite, Shibi Meyer, Kathrin Kaspar, Brian K. Cooper, Jonathan D. Wang, Shaomei Weimer, Jill M.