Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal
Titel:
Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal
Auteur:
Moscatelli, Ilana Almarza, Elena Schambach, Axel Ricks, David Schulz, Ansgar Herzog, Christopher D. Henriksen, Kim Askmyr, Maria Schwartz, Jonathan D. Richter, Johan