Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients
Titel:
Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients
Auteur:
Shi, Xiaoxia Aronson, Sem J. ten Bloemendaal, Lysbeth Duijst, Suzanne Bakker, Robert S. de Waart, Dirk R. Bortolussi, Giulia Collaud, Fanny Oude Elferink, Ronald P. Muro, Andrés F. Mingozzi, Federico Ronzitti, Giuseppe Bosma, Piter J.