Long-Term Therapeutic Efficacy of Intravenous AAV-Mediated Hamartin Replacement in Mouse Model of Tuberous Sclerosis Type 1
Titel:
Long-Term Therapeutic Efficacy of Intravenous AAV-Mediated Hamartin Replacement in Mouse Model of Tuberous Sclerosis Type 1
Auteur:
Prabhakar, Shilpa Cheah, Pike See Zhang, Xuan Zinter, Max Gianatasio, Maria Hudry, Eloise Bronson, Roderick T. Kwiatkowski, David J. Stemmer-Rachamimov, Anat Maguire, Casey A. Sena-Esteves, Miguel Tannous, Bakhos A. Breakefield, Xandra O.