Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
Titel:
Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
Auteur:
Spronck, Elisabeth A. Liu, Ying Poi Lubelski, Jacek Ehlert, Erich Gielen, Sander Montenegro-Miranda, Paula de Haan, Martin Nijmeijer, Bart Ferreira, Valerie Petry, Harald van Deventer, Sander J.