Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease
Titel:
Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease
Auteur:
Martier, Raygene Sogorb-Gonzalez, Marina Stricker-Shaver, Janice Hübener-Schmid, Jeannette Keskin, Sonay Klima, Jiri Toonen, Lodewijk J. Juhas, Stefan Juhasova, Jana Ellederova, Zdenka Motlik, Jan Haas, Eva van Deventer, Sander Konstantinova, Pavlina Nguyen, Huu Phuc Evers, Melvin M.