AAV Gene Therapy Utilizing Glycosylation-Independent Lysosomal Targeting Tagged GAA in the Hypoglossal Motor System of Pompe Mice
Titel:
AAV Gene Therapy Utilizing Glycosylation-Independent Lysosomal Targeting Tagged GAA in the Hypoglossal Motor System of Pompe Mice
Auteur:
Doyle, Brendan M. Turner, Sara M.F. Sunshine, Michael D. Doerfler, Phillip A. Poirier, Amy E. Vaught, Lauren A. Jorgensen, Marda L. Falk, Darin J. Byrne, Barry J. Fuller, David D.