Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs
Titel:
Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs
Auteur:
Majowicz, Anna Nijmeijer, Bart Lampen, Margit H. Spronck, Lisa de Haan, Martin Petry, Harald van Deventer, Sander J. Meyer, Christian Tangelder, Marco Ferreira, Valerie