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Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia |
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Titel: |
Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia |
Auteur: |
Lidonnici, Maria Rosa Paleari, Ylenia Tiboni, Francesca Mandelli, Giacomo Rossi, Claudia Vezzoli, Michela Aprile, Annamaria Lederer, Carsten Werner Ambrosi, Alessandro Chanut, Franck Sanvito, Francesca Calabria, Andrea Poletti, Valentina Mavilio, Fulvio Montini, Eugenio Naldini, Luigi Cristofori, Patrizia Ferrari, Giuliana |
Verschenen in: |
Molecular therapy. Methods & clinical development |
Paginering: |
Jaargang 11 (2018) nr. C pagina's 9-28 |
Jaar: |
2018 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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