An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models
Titel:
An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models
Auteur:
Gérard, Catherine Xiao, Xiao Filali, Mohammed Coulombe, Zoé Arsenault, Marie Couet, Jacques Li, Juan Drolet, Marie-Claude Chapdelaine, Pierre Chikh, Amina Tremblay, Jacques P