Proof of concept for AAV2/5-mediated gene therapy in iPSC-derived retinal pigment epithelium of a choroideremia patient
Titel:
Proof of concept for AAV2/5-mediated gene therapy in iPSC-derived retinal pigment epithelium of a choroideremia patient
Auteur:
Cereso, Nicolas Pequignot, Marie O Robert, Lorenne Becker, Fabienne De Luca, Valerie Nabholz, Nicolas Rigau, Valerie De Vos, John Hamel, Christian P Kalatzis, Vasiliki