Low-Dose Gene Therapy for Murine PKU Using Episomal Naked DNA Vectors Expressing PAH from Its Endogenous Liver Promoter
Title:
Low-Dose Gene Therapy for Murine PKU Using Episomal Naked DNA Vectors Expressing PAH from Its Endogenous Liver Promoter
Author:
Grisch-Chan, Hiu Man Schlegel, Andrea Scherer, Tanja Allegri, Gabriella Heidelberger, Raphael Tsikrika, Panagiota Schmeer, Marco Schleef, Martin Harding, Cary O. Häberle, Johannes Thöny, Beat