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One-Step Biallelic and Scarless Correction of a β-Thalassemia Mutation in Patient-Specific iPSCs without Drug Selection |
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Title: |
One-Step Biallelic and Scarless Correction of a β-Thalassemia Mutation in Patient-Specific iPSCs without Drug Selection |
Author: |
Liu, Yali Yang, Yi Kang, Xiangjin Lin, Bin Yu, Qian Song, Bing Gao, Ge Chen, Yaoyong Sun, Xiaofang Li, Xiaoping Bu, Lei Fan, Yong |
Appeared in: |
Molecular therapy - nucleic acids |
Paging: |
Volume 6 () nr. C pages 57-67 |
Year: |
2017 |
Contents: |
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Publisher: |
The Authors |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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