Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation
Titel:
Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation
Auteur:
Slijkerman, Radulfus WN Vaché, Christel Dona, Margo García-García, Gema Claustres, Mireille Hetterschijt, Lisette Peters, Theo A Hartel, Bas P Pennings, Ronald JE Millan, José M Aller, Elena Garanto, Alejandro Collin, Rob WJ Kremer, Hannie Roux, Anne-Françoise Van Wijk, Erwin
Verschenen in:
Molecular therapy - nucleic acids
Paginering:
Jaargang 5 () nr. C pagina's p.
Jaar:
2016
Inhoud:
Uitgever:
Official journal of the American Society of Gene & Cell Therapy