Splicing correction by peptide-conjugated morpholinos as a novel treatment for late-onset Pompe disease
Titel:
Splicing correction by peptide-conjugated morpholinos as a novel treatment for late-onset Pompe disease
Auteur:
Oliver, Ryan A. Ahern, Meghan E. Castaneda, Perla G. Jinadasa, Tushare Bardhan, Anirban Morgan, Kathy Y. Ha, Kristin Adhikari, Kailash Jungels, Nino Liberman, Noa Mitra, Anindita Greer, Christopher D. Wright, Alec M. Thompson, Emily G. Garcia, Stephanie Copson, Elena Allu, Senkara Tan, Xuyu Callahan, Alex J. Cai, Bao Zhong Guerlavais, Vincent Kim, Kevin J. Malmberg, Annika B.