CAG-targeted brain-permeable therapy tested in biallelic humanized polyQ mouse models
Titel:
CAG-targeted brain-permeable therapy tested in biallelic humanized polyQ mouse models
Auteur:
Surdyka, Magdalena Kalinowska-Pośka, Żaneta Niewiadomska-Cimicka, Anna Jesion, Ewelina Fiszer, Agnieszka Singer-Mikosch, Elisabeth Fievet, Lorraine Przybyl, Lukasz Caron, Nicholas S. Hayden, Michael R. Nguyen, Huu Phuc Trottier, Yvon Figiel, Maciej