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Efficient and in situ correction of hemoglobin Constant Spring mutation by prime editing in human hematopoietic cells |
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Titel: |
Efficient and in situ correction of hemoglobin Constant Spring mutation by prime editing in human hematopoietic cells |
Auteur: |
Shao, Congwen Liu, Qing Xu, Jinchao Zhang, Jianxiang Zhang, Chengpeng Xin, Ye Ye, Yuhua Lin, Bin Zhang, Xinhua Cheng, Li Xu, Xiangmin Xu, Peng |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 35 () nr. 4 pagina's p. |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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