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Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT |
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Titel: |
Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT |
Auteur: |
Iwamoto, Naoki Liu, Yuanjing Frank-Kamenetsky, Maria Maguire, Abbie Tseng, Wei Chou Taborn, Kristin Kothari, Nayantara Akhtar, Ali Bowman, Keith Shelke, Juili Dilip Lamattina, Anthony Hu, Xiao Shelley Jang, Hyun Gyung Kandasamy, Pachamuthu Liu, Fangjun Longo, Ken Looby, Richard Meena, Metterville, Jake Pan, Qianli Purcell-Estabrook, Erin Shimizu, Mamoru Prakasha, Priyanka Shiva Standley, Stephany Upadhyay, Hansini Yang, Hailin Yin, Yuan Zhao, Anderson Francis, Christopher Byrne, Mike Dale, Elena Verdine, Gregory L. Vargeese, Chandra |
Verschenen in: |
Molecular therapy - nucleic acids |
Paginering: |
Jaargang 35 () nr. 3 pagina's p. |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
The Author(s) |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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