Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants
Titel:
Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants
Auteur:
Knauer, Carolin Haltern, Henrike Schoger, Eric Kügler, Sebastian Roos, Lennart Zelarayán, Laura C. Hasenfuss, Gerd Zimmermann, Wolfram-Hubertus Wollnik, Bernd Cyganek, Lukas