Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression
Titel:
Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression
Auteur:
González-Martínez, Irene Cerro-Herreros, Estefanía Moreno, Nerea García-Rey, Andrea Espinosa-Espinosa, Jorge Carrascosa-Sàez, Marc Piqueras-Losilla, Diego Arzumanov, Andrey Seoane-Miraz, David Jad, Yahya Raz, Richard Wood, Matthew J. Varela, Miguel A. Llamusí, Beatriz Artero, Rubén